What Is Gene Therapy? Pros, Cons & Examples - Cleveland Clinic
Jun 17, 2025 · It works by replacing a malfunctioning gene, “turning off” a disease-causing gene or giving you a new copy of a gene. Approved gene therapies treat inherited blood, neuromuscular and …
Gene Therapies in Action: A Look at Examples of Successful Treatments
Let’s look at some real-life examples of successful gene therapies in these 4 main categories. Viral vector-based methods use a non-hazardous and non-replicating virus to transfer the DNA code for a …
List of gene therapies - Wikipedia
This article contains a list of commercially available gene therapies. Beremagene geperpavec (Vyjuvek): treatment of wounds. [2] Exagamglogene autotemcel (Casgevy): treatment for sickle cell disease. …
Gene therapy | Description, Uses, Examples, & Safety Issues - Britannica
Dec 9, 2025 · Some aspects of gene therapy, including genetic manipulation and selection, research on embryonic tissue, and experimentation on human subjects, have aroused ethical controversy and …
FDA Approved Gene Therapy Examples
Find examples of approved gene therapies in the U.S., when they were approved, and the diseases they were approved for.
Gene therapy - Mayo Clinic
Apr 23, 2024 · For example, a gene called p53 usually prevents tumor growth. Several types of cancer have been linked to problems with the p53 gene. If healthcare professionals could replace the faulty …
7 Gene Therapy Examples & Applications in Healthcare
Jan 19, 2018 · Without further ado, here’s taking a look at the greatest gene therapy examples and applications that have set the ball rolling for even bigger scientific breakthroughs. 1. CAR-Engineered …
Current State of Human Gene Therapy: Approved Products and Vectors
Presently, the gene therapy landscape stands adorned with 22 approved in vivo and ex vivo products, including IMLYGIC, LUXTURNA, Zolgensma, Spinraza, Patisiran, and many more.
What Are the Current FDA-Approved Gene Therapies?
An overview of approved gene therapies, detailing how they address conditions by replacing genes, editing cells, or delivering new genetic instructions.
Exploring gene therapy: Types, methods and applications | Abcam
Gene therapy employs techniques such as using viral vectors to transfer genes, CRISPR-Cas9 for precise gene editing, and non-viral methods such as electroporation or liposomes for gene delivery.